Found 12 matching trials
Pharmacokinetics, Pharmacodynamics And Safety Study Of Elelyso(tm) In Pediatric Subjects With Type 1 Gaucher Disease
PHASE4In August of 2014, the FDA approved ELELYSO for long-term enzyme replacemen...
A Multicenter Extension Study of Taliglucerase Alfa in Pediatric Subjects With Gaucher Disease
PHASE3A protocol to extend the assessment of the safety and efficacy of taligluce...
Location
Shaare Zedek Medical Center
A Multicenter, Safety and Efficacy Study of Taliglucerase Alfa in Subjects With Type 3 Gaucher Disease
PHASE4This is a multicenter study to assess the safety and efficacy of taliglucer...
Location
All India Institute of Medical Sciences
Assessing the Impact of Elelyso on Bone Involvement Currently Treated With Other ERTs
NAThe objective of this study is to assess Elelyso treatment on bone disease ...
Location
Multiple Locations
Switchover Trial From Imiglucerase to Plant Cell Expressed Recombinant Human Glucocerebrosidase
PHASE3This is a multi-center, open-label, switchover trial to assess the safety o...
Location
University Research Foundation for Lysosomal Storage Diseases, Inc.
Plant Cell Expressed Recombinant Human Glucocerebrosidase Extension Trial
PHASE3Gaucher disease, the most prevalent lysosomal storage disorder, is caused b...
Location
Department of Human Genetics, Emory University School of Medicine
Phase I Single Dose-Escalation Safety Study of Human Glucocerebrosidase (prGCD)
PHASE1Gaucher disease, the most prevalent lysosomal storage disorder, is caused b...
Location
Multiple Locations
A Multicenter Extension Study of Taliglucerase Alfa in Adult Subjects With Gaucher Disease
PHASE3This is a multi-center trial to further extend the assessment of the safety...
Location
Multiple Locations
An Efficacy and Safety Study of AVR-RD-02 Compared to Enzyme Replacement Therapy for Treatment of Gaucher Disease Type 3
PHASE2The purpose of this study is to evaluate the efficacy and safety of autolog...
Location
Multiple Locations
A Phase III Trial to Assess the Safety and Efficacy of Plant Cell Expressed GCD in Patients With Gaucher Disease
PHASE3Gaucher disease, the most prevalent lysosomal storage disorder, is caused b...
Location
University Research Foundation for Lysosomal Storage Diseases